Understanding the Human Brain and Disease

Genetic approaches and next-generation 3D human brain models to decode pediatric neurological disease.

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About the Lab

Decoding the genetic basis of brain disorders

The Chen Lab investigates the genetic mechanisms underlying pediatric neurodevelopmental disorders. Building on advances in multi-level in vitro and in vivo 3D cellular systems, we aim to investigate how disease-causing variants alter gene networks, cellular states, and circuit-level phenotypes in the developing human brain.

Live calcium imaging Human iPSC-derived neurons in culture — Chen Lab, St. Jude

Research Focus

Our scientific questions

We use human iPSC-derived neurons, brain organoids, and mouse models to study how genetic variants cause pediatric neurological disease.

01

Neurodevelopmental Disorders

Investigating the genetic underpinnings of autism spectrum disorder, intellectual disability, and epilepsy using patient-derived iPSC models and CRISPR genome editing.

ASD Epilepsy iPSC CRISPR
02

3D Brain Organoid Models

Developing next-generation cerebral organoid systems to model human brain development and disease in a dish, enabling high-throughput functional assays.

Organoids Brain-on-chip MEA Calcium Imaging
03

RNA Splicing & Gene Networks

Decoding how disease-causing variants disrupt RNA splicing networks and alter gene expression programs during human neurodevelopment.

RNA Splicing scRNA-seq SRRM2 Gene Networks
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Therapeutic Strategies

Translating mechanistic insights into therapeutic approaches, including antisense oligonucleotides, gene therapy vectors, and small molecule screens.

ASO AAV Drug Screen

Publications

Recent work

Selected publications from the Chen Lab. For a complete list, see Google Scholar.

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The Team

Meet the people

A diverse and passionate team of scientists working together to understand neurological disease.

News & Updates

Lab news

Latest updates from the Chen Lab.

June 2026

Chen Lab officially opens at St. Jude

The Chen Lab is now open at St. Jude Children's Research Hospital in the Department of Genomic and Translational Neuroscience. We are excited to begin our research program!

2024

New paper published in Nature

Our latest work on Timothy syndrome and human brain organoids is published in Nature. Congratulations to all co-authors!

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2024

Xiaoyu receives Shoshana Levy Early Career Award

Dr. Xiaoyu Chen is honored with the 2024–2025 Shoshana Levy Early Career Award from Stanford University (Anne Wojcicki Foundation).

Join Us

Be part of the mission

We are always looking for passionate scientists to join our team. St. Jude offers exceptional resources, mentorship, and a collaborative environment.

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Graduate Students
We accept rotation students through the St. Jude Graduate School of Biomedical Sciences and the University of Tennessee Health Science Center.
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Postdoctoral Fellows
We seek creative and rigorous postdoctoral scientists with backgrounds in neuroscience, genomics, stem cell biology, or computational biology.
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Research Scientists
Experienced research scientists with strong technical skills in cell culture, molecular biology, or bioinformatics are encouraged to reach out.
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Contact

Get in touch

We welcome inquiries from prospective lab members, collaborators, and the press. Please reach out by email.

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Location Center for Pediatric Neurological Disease Research (CPNDR)
Department of Cell & Molecular Biology
St. Jude Children's Research Hospital
262 Danny Thomas Place, Memphis, TN 38105
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St. Jude Children's Research Hospital
Memphis, Tennessee